Showing posts with label Sanfilippo disease. Show all posts
Showing posts with label Sanfilippo disease. Show all posts

Friday, February 17, 2017

Research study testing new treatment for Sanfilippo disease progressing well

Manchester: A study into a new treatment for Sanfilippo disease, a rare and fatal condition which causes progressive dementia in children, is progressing well with results set to be published later this year. Also known as Mucopolysaccharidosis (MPS) III, there is currently no effective treatment for the condition which affects around 150 children in the UK.